The article I read recently explained that the NHS had agreed a different (undisclosed) amount of money for the treatment, and also explained that they balanced the cost of the drug against the cost of treating a person who then would develop the disease, and, of course, the emotional impact of a child's death. I suspect that care costs must be particularly high for this kind of treatment to be funded. Obviously I'm speaking as someone from the UK, where we don't just allow people to die if they don't have enough money to afford care. How the USA will approach this will be interesting.
Munchies2015 t1_j8o4anw wrote
Reply to comment by TrenchantPergola in Recently a gene therapy for a rare inherited neurodegenerative disorder was approved. How come cure is achieved through bone marrow transplantation? by nickoskal024
The article I read recently explained that the NHS had agreed a different (undisclosed) amount of money for the treatment, and also explained that they balanced the cost of the drug against the cost of treating a person who then would develop the disease, and, of course, the emotional impact of a child's death. I suspect that care costs must be particularly high for this kind of treatment to be funded. Obviously I'm speaking as someone from the UK, where we don't just allow people to die if they don't have enough money to afford care. How the USA will approach this will be interesting.